RARECast

548 Epizód

1. Accelerating the Development of Genetic Medicines with AI

   Közzétéve: 2023. 12. 07.
2. Leveraging AI to Address the Neuropsychiatric Conditions Associated with a Rare Disease

   Közzétéve: 2023. 11. 30.
3. In Pursuit of a Treatment for His Son, A Lawyer Becomes a Biotech Executive

   Közzétéve: 2023. 11. 22.
4. In Push for Treatment, a Patient Organization Becomes a Trial Sponsor

   Közzétéve: 2023. 11. 16.
5. Delayed Diagnosis of Rare Diseases Takes Staggering Economic Toll

   Közzétéve: 2023. 11. 09.
6. A Cell Therapy to Control Heart-Damaging Inflammation in Duchenne

   Közzétéve: 2023. 11. 02.
7. Stimulating the Growth of Muscle Mass in People with Neuromuscular Diseases

   Közzétéve: 2023. 10. 26.
8. Turning Grief into Action

   Közzétéve: 2023. 10. 19.
9. A Plea to the FDA to Give an Ultra-Rare Disease Drug a Fair Hearing

   Közzétéve: 2023. 10. 12.
10. How the Woolly Mammoth Beat a Path to Better Gene Therapies

    Közzétéve: 2023. 10. 05.
11. A Genetic Counselor’s Journey into Patient Advocacy

    Közzétéve: 2023. 09. 28.
12. A Company in the Fold of Rare Disease

    Közzétéve: 2023. 09. 21.
13. Disabling Antibodies that Drive Rare, Immunological Conditions

    Közzétéve: 2023. 09. 14.
14. Keeping the Sentinels of the Brain Vigilant

    Közzétéve: 2023. 09. 07.
15. Considering the Unfinished Work in Cystic Fibrosis

    Közzétéve: 2023. 08. 31.
16. How to Advocate for Yourself as You Battle Cancer

    Közzétéve: 2023. 08. 24.
17. Targeting Neuroinflammation to Treat ALS

    Közzétéve: 2023. 08. 17.
18. Leveraging Community Partnerships to Address a Rare Disease Behind a Medical Mystery in New Mexico

    Közzétéve: 2023. 08. 10.
19. Accelerating Gene Editing Therapies for Rare, Neurological Conditions

    Közzétéve: 2023. 08. 03.
20. Inhibiting Electrical Activity in Rare, Seizure Disorders

    Közzétéve: 2023. 07. 27.