548 Epizód

  1. A Heart Attack that Led to a Rare Disease Diagnosis

    Közzétéve: 2025. 01. 30.

  2. Targeting Rare Liver Diseases with Gene Editing Therapies

    Közzétéve: 2025. 01. 23.

  3. Using AI to De-Risk Rare Disease Drug Development

    Közzétéve: 2025. 01. 16.

  4. Addressing a Growing Demand for Plasma-Derived Therapies

    Közzétéve: 2025. 01. 09.

  5. Empowering Patients with Data to Drive Drug Development

    Közzétéve: 2025. 01. 02.

  6. How Advocates Are Advancing a Treatment for an Ultra-Rare Disease

    Közzétéve: 2024. 12. 26.

  7. Engineering B Cells to Produce Therapeutic Proteins

    Közzétéve: 2024. 12. 19.

  8. A Pipeline Win as BridgeBio Learns to Balance Theory with Practice

    Közzétéve: 2024. 12. 12.

  9. Considering What It Will Take for Payers to Embrace Advances in Sequencing

    Közzétéve: 2024. 12. 05.

  10. Finding Strength

    Közzétéve: 2024. 11. 27.

  11. A Non-Profit Works to Advance a DMD Gene Therapy

    Közzétéve: 2024. 11. 21.

  12. Accepting What We Can’t Understand

    Közzétéve: 2024. 11. 14.

  13. A Gene Therapy Company Born from a Father’s Efforts to Save his Daughter

    Közzétéve: 2024. 11. 07.

  14. Lowering Barriers to Clinical Trial Participation with Do-It-Yourself Blood Sample Collection

    Közzétéve: 2024. 10. 31.

  15. Scaling N-of-1 Therapies to Viability

    Közzétéve: 2024. 10. 24.

  16. Building Gene Therapies that Address Gain and Loss of Function Simultaneously

    Közzétéve: 2024. 10. 17.

  17. How One Woman Climbed from Patient to Advocate

    Közzétéve: 2024. 10. 10.

  18. Shortening the Diagnostic Odyssey

    Közzétéve: 2024. 10. 03.

  19. Making Exomes More Revealing

    Közzétéve: 2024. 09. 26.

  20. How One Patient Organization Catalyzed Drug Development

    Közzétéve: 2024. 09. 19.

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RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.

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